A patient death in a CRISPR trial halts gene editing studies, raising critical safety questions. What this means for the ...

This virtual event is part of the Transforming Pediatric Healthcare series from U.S. News & World Report, developed with ...

A new CRISPR breakthrough shows scientists can turn genes back on without cutting DNA, by removing chemical tags that act ...

A five-year-old boy who received the world's most expensive drug as a baby has made "incredible progress" and can walk ...

The use of base editing to generate universal off-the-shelf CAR T cells induced durable remissions -- up to 36 months in one ...

GEN’s first virtual event of 2026—we present a group of outstanding researchers and thought-leaders to discuss the latest advances and challenges in delivering genetic therapies.

This story is part of a series on the current progression in Regenerative Medicine. In 1999, I defined regenerative medicine as the collection of interventions that restore tissues and organs damaged ...

Impella, which J&J touts as the world’s smallest heart pump, has a range of devices used for various heart conditions. Lexeo ...

A new treatment might just be hope for many people living with chronic pain. In a recent preclinical study, researchers ...

A heart attack survivor is the first person to receive groundbreaking gene therapy which aims to prevent a major heart ...

A preclinical study uncovered a new gene therapy that targets pain centers in the brain while eliminating the risk of ...

While gene therapy for cystic fibrosis is still in the research phase, researchers aim to correct the defective gene responsible for the disease. Current research is promising. Cystic fibrosis (CF) is ...